Ear, Nose And Throat
One of the First Children in the Nation to Receive a New Gene Therapy is Now Waiting to Hear
Ricky has a rare form of genetic deafness. After becoming the first child in New York to receive a newly approved gene therapy at NewYork-Presbyterian, his family and doctors are awaiting signs of a world he has never heard.
Sickle Cell
FDA Approves First Gene Therapies to Treat Sickle Cell Disease
One of the treatments, CASGEVY, is the first approved therapy in the United States to use CRISPR gene-editing technology.
Sickle Cell
Can Gene Therapy Cure Patients with Sickle Cell Disease?
An experimental trial shows promise for patients with a life-threatening inherited blood disorder.
