Sickle Cell
FDA Approves First Gene Therapies to Treat Sickle Cell Disease
One of the treatments, CASGEVY, is the first approved therapy in the United States to use CRISPR gene-editing technology.
Patient Stories
After Beating Sickle Cell Disease, This College Student Has Big Plans for the Future
Francisca Kwakye left Ghana as a young child to receive life-changing treatment for sickle cell disease. Now cured, her dream is to improve health care access for others.
Sickle Cell
Can Gene Therapy Cure Patients with Sickle Cell Disease?
An experimental trial shows promise for patients with a life-threatening inherited blood disorder.
