Gene Therapy Program

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gene therapy
gene therapy

Treating genetic disease at its source

Gene therapy targets genetic disease at its root by rewriting the code, not just treating its symptoms. At NewYork-Presbyterian, our researchers have been at the forefront of this revolution for over a decade. Today, we continue to be global leaders in gene therapy, exploring bold new approaches to tackle inherited conditions in both children and adults.

More about gene therapy
Dr. Frey with patient

Our comprehensive care team for gene therapy

With years of experience and deep expertise, our dedicated care team guides you through each stage of gene therapy, ensuring a seamless, fully supported experience from evaluation through recovery. Backed by a multidisciplinary team of specialists, support is continuous, integrated, and tailored to you.

Clinical trials for gene therapy

We’re highly committed to gene therapy research to improve its effectiveness, reduce side effects, and extend its benefits to people with other cancers. Our programs have an onsite facility to manufacture new cell therapies, and we are working on clinical trials to bring these treatments to more patients in need.

Clinical trials at Weill Cornell Medicine
Clinical trials at Columbia University

Insurance eligibility for gene therapy

Our team helps patients navigate the complex insurance and authorization process that can come with advanced therapies. With experience working across major payers and securing access to high-cost treatments, we help make the path to care as smooth and timely as possible.

For clinicians

Our clinicians page on advanced therapies provides information on specific drug therapies, how to refer a patient, and patient journey expectations.

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