Gene Therapy

An international leader in gene therapy

Gene therapy targets genetic disease at its root by rewriting the code, not just treating its symptoms. At NewYork-Presbyterian/Columbia University Irving Medical Center, our researchers have been at the forefront of this revolution for over a decade by pioneering gene therapy for sickle cell disease. Today, we continue to be global leaders in gene therapy, exploring bold new approaches to tackle inherited conditions in both children and adults.

A world-class team of gene therapy experts

Our team brings together leading specialists with decades of experience in bone marrow transplantation and cellular therapies for genetic diseases. By applying their deep expertise, they not only advance cutting-edge gene therapy approaches — they are fully equipped to manage any side effects or complications that may arise, ensuring patients receive the safest, most comprehensive care possible.

Our team also understands the toll that sickle cell disease and other chronic genetic illnesses take on the lives of patients and their families, including their mental health. A dedicated psychiatrist is available to provide psychological support.

Find gene therapy at NewYork-Presbyterian

It’s important to get gene therapy from a center that has a multidisciplinary team well-versed in the nuances of stem cell transplantation for sickle cell disease, and is able to provide leading-edge therapies to address infections and other possible complications. You can find that team at NewYork-Presbyterian/Columbia.